Genomics England – Pilot launched to support children with rare conditions to access personalised therapies (from Catapult’s regulatory round-up – December 2023)
The UK government has announced its support for the Rare Therapies Launch Pad, a new programme that will develop a pathway for children with rare conditions to access individualised therapies. The programme’s first project will explore the use of individualised therapies known as antisense oligonucleotides (ASOs) to treat children with ultra-rare and life-threatening brain conditions.
In the future, the Rare Therapies Launch Pad will support access to other types of individualised therapies across a wider range of rare conditions.
Please find further information here.
Published on the 5th of january 2024. Read all of Catapult’s regulatory round-up here.
OpenEdition vous propose de citer ce billet de la manière suivante :
adelage (21 mai 2024). Genomics England – Pilot launched to support children with rare conditions to access personalised therapies (from Catapult’s regulatory round-up – December 2023). ELSIBI. Consulté le 16 janvier 2025 à l’adresse https://doi.org/10.58079/11p1e
